Caden Major was born with sickle cell disease – an inherited blood disorder affecting red blood cells. Now at 19 years old, ...
There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University's College ...
A 16-year-old with a rare blood disease was cured with innovative gene therapy by doctors at the Children’s Hospital at ...
Major is one of the first pediatric patients in Florida to receive gene therapy for sickle cell disease since the FDA ...
In a new study, scientists at the Max Planck Institute for Evolutionary Anthropology in Leipzig analyzed the impact of more ...
Researchers at the Icahn School of Medicine at Mount Sinai have developed a first-of-its-kind mRNA system that switches on therapeutic genes preferentially inside targeted cells—an advance ...
There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University’s College ...
Mount Sinai scientists developed V2P, a powerful new AI tool that predicts how specific DNA mutations translate into disease, ...
In the big picture, matched sibling donor transplants remain the standard of care, Boelens said. But gene therapy is ...
A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a ...
As of Friday, December 12, Tenaya Therapeutics, Inc.’s TNYA share price has dipped by 32.45%, which has investors questioning ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback