Scientists at the University College London (UCL) have developed a novel therapy that helps treat patients with T cell acute ...

Researchers created a highly efficient gene-editing method that fixes multiple DNA mutations in a single step. The breakthrough could revolutionize genetic medicine by making treatments for complex ...

Scientists looked at multiple techniques used to measure the modified viruses deployed in some gene therapy research and treatments. One technique, known as SEC-MALS, was the most precise and accurate ...

Doctors have discovered that a new groundbreaking therapy has reversed incurable blood cancers in some patients.A therapy, ...

This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...

Analyzing the purity of adeno-associated virus (AAV)-based gene therapy products requires effective methods for detecting host proteins, DNA, and incomplete viral particles in samples. It is a ...

Researchers at the University of Geneva, together with colleagues in Switzerland, France, the United States and Israel, ...

Over the last four years, Shriners Children’s St. Louis researchers have been working to develop a new way to prevent the effects of childhood obesity. Now, using gene therapy, Shriners Children’s St.

While gene therapy for cystic fibrosis is still in the research phase, researchers aim to correct the defective gene responsible for the disease. Current research is promising. Cystic fibrosis (CF) is ...

A Yale research team has created a new computer tool that can pinpoint when exactly genes turn on and off over time during brain development - a finding that may one day help doctors identify the ...

The gene therapy market presents key opportunities in addressing genetic disorders by targeting the root cause through therapies like gene augmentation. North America leads in market share, with ...

Oliver has an inherited condition called Hunter syndrome, which causes progressive damage to the body and brain.